Neuren Pharmaceuticals

Neuren is a biopharmaceutical company based in Camberwell, Victoria, Australia. It is focused on developing drugs for multiple serious neurological disorders that emerge in early childhood, including Rett syndrome, Phelan-McDermid syndrome, Angelman syndrome, and Pitt Hopkins syndrome. The company's lead drug, Daybue™ (trofinetide), is the only FDA-approved treatment for Rett syndrome.